Defining SOD1 ALS natural history to guide therapeutic clinical trial design
Taha Bali, Wade Self, Jingxia Liu, Teepu Siddique, Leo H Wang, Thomas D Bird, Elena Ratti, Nazem Atassi, Kevin B Boylan, Jonathan D Glass, Nicholas J Maragakis, James B Caress, Leo F McCluskey, Stanley H Appel, James P Wymer, Summer Gibson, Lorne Zinman, Tahseen Mozaffar, Brian Callaghan, April L McVey, Jennifer Jockel-Balsarotti, Peggy Allred, Elena R Fisher, Glenn Lopate, Alan Pestronk, Merit E Cudkowicz, Timothy M Miller
Journal of Neurology, Neurosurgery & Psychiatry Feb 2017, 88 (2) 99-105; DOI: 10.1136/jnnp-2016-313521