L4 Sustained and strong HTT silencing by AAV5-miHTT as therapy for huntington’s disease

Melvin Evers; Jana Miniarikova; Bas Blits; Lisa Spronck; Cynthia Brouwers; Nicole Déglon; Jan Motlik; Krystof Bankiewicz; Amber Southwell; Martin de Haan; Charles Richard; Harald Petry; Pavlina Konstantinova

doi:10.1136/jnnp-2016-314597.259

Article info

Experimental Therapeutics – Preclinical

L4 Sustained and strong HTT silencing by AAV5-miHTT as therapy for huntington’s disease

Authors

Melvin Evers 1Department of Research and Development, uniQure N.V., Amsterdam, The Netherlands PubMed articles Google scholar articles
Jana Miniarikova 1Department of Research and Development, uniQure N.V., Amsterdam, The Netherlands PubMed articles Google scholar articles
Bas Blits 1Department of Research and Development, uniQure N.V., Amsterdam, The Netherlands PubMed articles Google scholar articles
Lisa Spronck 1Department of Research and Development, uniQure N.V., Amsterdam, The Netherlands PubMed articles Google scholar articles
Cynthia Brouwers 1Department of Research and Development, uniQure N.V., Amsterdam, The Netherlands PubMed articles Google scholar articles
Nicole Déglon 2Laboratory of Cellular and Molecular Neurotherapies, Lausanne University Hospital, Switzerland PubMed articles Google scholar articles
Jan Motlik 3Institute of Animal Physiology and Genetics, Liběchov, Czech Republic PubMed articles Google scholar articles
Krystof Bankiewicz 4Department of Neurosurgery, University of California San Francisco, USA PubMed articles Google scholar articles
Amber Southwell 5Centre for Molecular Medicine and Therapeutics, University of British Columbia, Vancouver, Canada PubMed articles Google scholar articles
Martin de Haan 1Department of Research and Development, uniQure N.V., Amsterdam, The Netherlands PubMed articles Google scholar articles
Charles Richard 1Department of Research and Development, uniQure N.V., Amsterdam, The Netherlands PubMed articles Google scholar articles
Harald Petry 1Department of Research and Development, uniQure N.V., Amsterdam, The Netherlands PubMed articles Google scholar articles
Pavlina Konstantinova 1Department of Research and Development, uniQure N.V., Amsterdam, The Netherlands PubMed articles Google scholar articles

Citation

Evers M, Miniarikova J, Blits B, et al

L4 Sustained and strong HTT silencing by AAV5-miHTT as therapy for huntington’s disease

Journal of Neurology, Neurosurgery & Psychiatry 2016;87:A91.

Publication history

First published September 13, 2016.

Online issue publication

February 07, 2017

Request permissions

If you wish to reuse any or all of this article please use the link below which will take you to the Copyright Clearance Center’s RightsLink service. You will be able to get a quick price and instant permission to reuse the content in many different ways.

Main menu

Authors

Citation

Publication history

Request permissions

Copyright information

Log in using your username and password

Main menu

Log in using your username and password

You are here

Authors

Citation

Publication history

Request permissions

Copyright information

Read the full text or download the PDF:

Log in using your username and password