Nusinersen for SMA: expanded access programme
Michelle A Farrar, Hooi Ling Teoh, Kate A Carey, Anita Cairns, Robin Forbes, Karen Herbert, Sandra Holland, Kristi J Jones, Manoj P Menezes, Margot Morrison, Kate Munro, Daniella Villano, Richard Webster, Ian R Woodcock, Eppie M Yiu, Hugo Sampaio, Monique M Ryan
Journal of Neurology, Neurosurgery & Psychiatry Sep 2018, 89 (9) 937-942; DOI: 10.1136/jnnp-2017-317412