EVALUATION OF FUNCTIONAL OUTCOME MEASURES AS A SURROGATE MARKER OF DISEASE SEVERITY IN PATIENTS WITH MITOCHONDRIAL DISEASE
Jane Newman, Brook Galna, Djordje Jakovljevic, Matthew Bates, Andrew Schaefer, Robert McFarland, Douglass Turnbull, Michael Trenell, Lynn Rochester, Grainne Gorman
Journal of Neurology, Neurosurgery & Psychiatry Nov 2013, 84 (11) e2; DOI: 10.1136/jnnp-2013-306573.199