PATISIRAN PH 2 OPEN-LABEL EXTENSION STUDY IN FAMILIAL AMYLOIDOTIC POLYNEUROPATHY
Hartmut Schmidt, David Adams, Teresa Coelho, Isabel Conceicao, Marcia Waddington-Cruz, Juan Buades, Josep Campistol, Jean Pouget, Jared Gollob, Ole Suhr
Journal of Neurology, Neurosurgery & Psychiatry Dec 2016, 87 (12) e1; DOI: 10.1136/jnnp-2016-315106.29