15.33 AVXS-101 in presymptomatic spinal muscular atrophy (SMA)

Kevin A Strauss; Kathryn J Swoboda; Michelle A Farrar; Hugh J McMillan; Julie Parsons; Jena M Krueger; Susan T Iannaccone; Claudia A Chiriboga; Jennifer M Kwon; Kayoko Saito; Mariacristina Scoto; Imran Kausar; Meredith Schultz; Elaine Kernbauer; Marcia Farrow; Francis G Ogrinc; Sarah Kavanagh; Douglas E Feltner; Bryan E McGill; Sidney A Spector; James L’Italien; Douglas M Sproule; Francesco Muntoni

doi:10.1136/jnnp-2019-ABN-2.20

Article info

Parallel session 4: Treatments; looking to the future

15.33 AVXS-101 in presymptomatic spinal muscular atrophy (SMA)

Authors

Kevin A Strauss Clinic for Special Children, Strasburg, PA, USA PubMed articles Google scholar articles
Kathryn J Swoboda Department of Neurology, Massachusetts General Hospital, Boston, MA, USA PubMed articles Google scholar articles
Michelle A Farrar Department of Neurology, Sydney Children’s Hospital Network, Randwick, NSW, Australia PubMed articles Google scholar articles
Hugh J McMillan Department of Pediatrics, Children’s Hospital of Eastern Ontario, Ottawa, Canada PubMed articles Google scholar articles
Julie Parsons Department of Pediatrics, University of Colorado School of Medicine, Aurora, CO, USA PubMed articles Google scholar articles
Jena M Krueger Department of Neurology, Helen DeVos Children’s Hospital, Grand Rapids, MI, USA PubMed articles Google scholar articles
Susan T Iannaccone Department of Pediatrics, University of Texas Southwestern Medical Center, Dallas, TX, USA PubMed articles Google scholar articles
Claudia A Chiriboga Division of Pediatric Neurology, Columbia University Medical Center, New York, NY, USA PubMed articles Google scholar articles
Jennifer M Kwon Department of Neurology, University of Wisconsin School of Medicine and Public Health, Madison, WI, USA PubMed articles Google scholar articles
Kayoko Saito Institute of Medical Genetics, Tokyo Women’s Medical University, Tokyo, Japan PubMed articles Google scholar articles
Mariacristina Scoto The Dubowitz Neuromuscular Centre, University College London, Great Ormond Street Institute of Child Health and Great Ormond Street Hospital, London, UK PubMed articles Google scholar articles
Imran Kausar AveXis, Inc., Bannockburn, IL, USA PubMed articles Google scholar articles
Meredith Schultz AveXis, Inc., Bannockburn, IL, USA PubMed articles Google scholar articles
Elaine Kernbauer AveXis, Inc., Bannockburn, IL, USA PubMed articles Google scholar articles
Marcia Farrow AveXis, Inc., Bannockburn, IL, USA PubMed articles Google scholar articles
Francis G Ogrinc AveXis, Inc., Bannockburn, IL, USA PubMed articles Google scholar articles
Sarah Kavanagh AveXis, Inc., Bannockburn, IL, USA PubMed articles Google scholar articles
Douglas E Feltner AveXis, Inc., Bannockburn, IL, USA PubMed articles Google scholar articles
Bryan E McGill AveXis, Inc., Bannockburn, IL, USA PubMed articles Google scholar articles
Sidney A Spector AveXis, Inc., Bannockburn, IL, USA PubMed articles Google scholar articles
James L’Italien AveXis, Inc., Bannockburn, IL, USA PubMed articles Google scholar articles
Douglas M Sproule AveXis, Inc., Bannockburn, IL, USA PubMed articles Google scholar articles
Francesco Muntoni The Dubowitz Neuromuscular Centre, University College London, Great Ormond Street Institute of Child Health and Great Ormond Street Hospital, London, UK National Institute of Health Research, Great Ormond Street Hospital Biomedical Research Centre, London, UK PubMed articles Google scholar articles

Citation

Strauss KA, Swoboda KJ, Farrar MA, et al

15.33 AVXS-101 in presymptomatic spinal muscular atrophy (SMA)

Journal of Neurology, Neurosurgery & Psychiatry 2019;90:e7.

Publication history

First published November 14, 2019.

Online issue publication

April 06, 2020

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