Genotype–phenotype correlation and treatment effects in young patients with GNAO1-associated disorders
Moritz Thiel, Daniel Bamborschke, Wibke G. Janzarik, Birgit Assmann, Simone Zittel, Steffi Patzer, Andrea Auhuber, Joachim Opp, Eva Matzker, Andrea Bevot, Juergen Seeger, Andreas van Baalen, Burkhard Stüve, Knut Brockmann, Sebahattin Cirak, Anne Koy
Journal of Neurology, Neurosurgery & Psychiatry Oct 2023, 94 (10) 806-815; DOI: 10.1136/jnnp-2022-330261