I02 A CAG repeat-targeting artificial miRNA lowers the mutant huntingtin level in the YAC128 model of huntington’s disease
Marta Olejniczak, Anna Kotowska-Zimmer, Lukasz Przybyl, Marianna Pewińska, Joanna Suszynska-Zajczyk, Dorota Wronka, Maciej Figiel
Journal of Neurology, Neurosurgery & Psychiatry Sep 2021, 92 (Suppl 1) A48; DOI: 10.1136/jnnp-2021-EHDN.116