Molecular Cell
Volume 68, Issue 3, 2 November 2017, Pages 479-490.e5
ArticleImpeding Transcription of Expanded Microsatellite Repeats by Deactivated Cas9
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Graphical Abstract
Keywords
RNA polymerase II
transcription
microsatellite repeat disease
myotonic dystrophy
amyotrophic lateral sclerosis
CRISPR
Cas9
C9ORF72/ALS/FTD
RNA toxicity
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